Prion Disease Treatment: Breakthroughs in Gene Editing

April 7, 2025

Prion disease treatment has emerged as a beacon of hope for those afflicted by these rare but devastating disorders caused by misfolded prion proteins in the brain.Recent research highlights the promising applications of gene editing therapy, which aims to directly alter the genetic underpinnings of conditions like Creutzfeldt-Jakob disease and fatal familial insomnia.
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